Safety, Efficacy, Pharmacokinetics, and Pharmacodynamics of NNZ-2591 in Children and Adolescents With Pitt Hopkins Syndrome  
 
    Development of Clinician- and Caregiver-Reported Outcome Measures for Evaluating Pitt Hopkins Syndrome  
 
    NNZ-2591, a Synthetic IGF-1 Metabolite Analog: Phase 2 Clinical Trial Results for Children and Adolescents With Pitt Hopkins Syndrome